AON-induced splice-switching and DMPK pre-mRNA degradation as potential therapeutic approaches for Myotonic Dystrophy type 1
Authors: Ewa Stepniak-Konieczna, Patryk Konieczny, Piotr Cywoniuk, Julia Dluzewska, Krzysztof Sobczak
Published in: Nucleic Acids Research
Publication type: article
Subject areas: Biochemistry, Genetics and Molecular Biology
SJR best quartile: Q1