Artificial miRNAs targeting CAG repeat expansion in ORFs cause rapid deadenylation and translation inhibition of mutant transcripts
Authors: Adam Ciesiolka, Anna Stroynowska-Czerwinska, Paweł Joachimiak, Agata Ciolak, Emilia Kozlowska, Michal Michalak, Magdalena Dabrowska, Marta Olejniczak, Katarzyna D Raczynska, Dominika Zielinska, Magdalena Wozna-Wysocka, Wlodzimierz J Krzyzosiak, Agnieszka Fiszer
Published in: Cellular and Molecular Life Sciences
Publication type: article
Subject areas: Biochemistry, Genetics and Molecular Biology; Neuroscience; Pharmacology, Toxicology and Pharmaceutics
SJR best quartile: Q1