AON-induced splice-switching and DMPK transcript degradation as therapeutic approaches for Myotonic Dystrophy type 1 (DM1)
Authors: Ewa Stepniak-Konieczna, Patryk Konieczny, Julia Zielinska, Krzysztof Sobczak
Published in: RNA 2018 - The 23rd Annual Meeting of The RNA Society
Publication type: conference