tbuckley/cabot-search huggingface dataset:
Subclassification of Erdheim-Chester Disease: Distinct Clinical and Molecular Findings between Classical and Non-Classical Forms
Authors: Dongni Yi, Ronald S Go, Gordon J Ruan, N. Nora Bennani, Mithun V Shah, Karen L Rech, Aishwarya Ravindran, Jay H Ryu, Robert Vassallo, Matthew J Koster, Caroline J Davidge-Pitts, Lucinda M Gruber, William Oliver Tobin, Julio C Sartori Valinotti, Talal Hilal, Liuyan Jiang, Muhamad Alhaj Moustafa, Asra Z. Ahmed, Gaurav Goyal, Jithma P Abeykoon
Journal: Blood (2024)
<i>Title: In Vivo Clonal Tracing of Hematopoietic Stem and Progenitor Cells Reveals Increased Clonal Heterogeneity during Aging, Alongside Critical Changes in Selection Patterns</i>
Authors: Lamis Naddaf, Marco De Dominici, Xiaowen Chen, Parveen Kumar, James S Chavez, Travis Roeder, Shilpita Karmakar, Eric M. Pietras, Hideyuki Oguro, James DeGregori, Sheng Li
Journal: Blood (2024)
Disparities in AML Survival in the Targeted Therapy Era: Real World Evidence of Enhanced Equity of Outcomes for Patients in Medically Underserved Areas
Authors: Fatima Tuz Zahra, Faustine Ong, Moazzam Shahzad, Onyee Chan, Najla H. Al Ali, Jeffrey E Lancet, Alison R. Walker, David Sallman, Rami S. Komrokji, Seongseok Yun, Andrew T. Kuykendall, Eric Padron, Zhuoer Xie
Journal: Blood (2024)
5-Year Follow-up of the Phase 2 Optic Study in Patients with Chronic-Phase Chronic Myeloid Leukemia: Efficacy, Safety, and First End-of-Treatment Mutational Results
Authors: Jorge E. Cortes, Michael W. Deininger, Jane Apperley, Chrisopher Kevin Arthur, Charles Chuah, Andreas Hochhaus, Hugues de Lavallade, Jeffrey H. Lipton, Elza Lomaia, James McCloskey, Michael J. Mauro, Beatriz Moiraghi, Carolina Pavlovsky, Gianantonio Rosti, Philippe Rousselot, Maria Undurraga, Lin Yang, Alexander Vorog, Tammie Yeh, L. Evan Reddick, Niti Patel, Hagop M. Kantarjian
Journal: Blood (2024)
Delays to Diagnosis of Peripheral T-Cell Lymphoma and Clinical Utility of Molecular Profiling: A UK Multicentre Real-World Study
Authors: Jesca Boot, Elizabeth Nelmes, Findlay Bewicke-Copley, Krushika Paleja, Emily Davenport, Ross Henderson, William Hann, Xiao-Yin Zhang, Hannah Bielby, Harshita Goradia, Naim Rahimi, Amjad Hmaid, Rumman Fatima Nizam, Imogen Welding, Vivek Radhakrishnan, Callum Harris, Danielle Monteil, Andrew Clear, Maria Calaminici, Paul Greaves, Andrew J. Davies, Graham P. Collins, Matthew R Wilson, Jeffery Smith, Christopher P Fox, Wendy Osborne, Lucy Cook, Matthew Ahearne, Kate Cwynarski, John G. Gribben, Jessica Okosun
Journal: Blood (2024)
A Phase 1, Open-Label, Dose Escalation and Dose Expansion Study of Cln-049 for the Treatment of Acute Myeloid Leukemia Patients with Measurable Residual Disease
Authors: Jonas S. Heitmann, Juliane S. Walz, Helmut R. Salih, Klaus H Metzeler, Daniel Heudobler, Felicitas R Thol, Hermann Einsele, Veit L. Buecklein, Pau Montesinos, Ana Alfonso Pierola, Gala Vega, Eduardo Rodriguez Arboli, Juan Miguel Bergua Burgues, Suhail Chaudhry, Judith Inumerable, Todd Shearer, Laura Liu, Sandeep Kaur, Kaida Wu, Marion Subklewe
Journal: Blood (2024)
Platelet Laboratory Markers of Failure of First-Line Treatments in Immune Thrombocytopenia (ITP)
Authors: Bianca Clerici, Claudia Ghali, Mariangela Scavone, Antonella Fioretti, Elena Giovanna Bossi, Simone Birocchi, Giovanna D'Avanzo, Monica Carpenedo, Sabrina Caberlon, Gian Marco Podda
Journal: Blood (2024)
Impact of FLT3 Inhibitor Maintenance Therapy on Post-Transplant Outcomes in FLT3-Mutated AML Patients: A Real World Analysis from the German Registry for Hematopoietic Stem Cell Transplantation and Cell Therapy (DRST)
Authors: Radwan Massoud, Sarah Flossdorf, Franziska Hanke, Thomas Schroeder, Wolfgang Andreas Bethge, Robert Zeiser, Caroline Pabst, Gerald Wulf, Elisa Sala, Inken Hilgendorf, Christof Scheid, Matthias Edinger, Friedrich Stölzel, Igor Wolfgang Blau, Matthias Stelljes, Guido Kobbe, Uwe Platzbecker, Jörg Bittenbring, Matthias Eder, Katharina Fleischhauer, Andreas Burchert, Christoph Schmid, Nicolaus Kroeger
Journal: Blood (2024)
A Novel JAK2 Inhibitor OB756 in Treatment of Janus Kinase Inhibitor-Naive Patients with Myelofibrosis: A Phase 1/2, Open-Label, Multicenter Study
Authors: Yile Zhou, Jian Huang, Bingbing Wen, Hu Zhou, Wei Yang, Lianlian Fan, Tiejun Gong, Sujun Gao, Zongjiu Jiao, Qingchi Liu, Lidong Zhao, Guocai Wu, Cuicui Wu, Jun Wang, Jin Zhang, Jiaping Fu, Zengmei Sheng, Zunmin Zhu, Jian Lu, Yi Zhang, Jie Jin
Journal: Blood (2024)
Trial in Progress: Cureaa - a Clinical Trial of Upfront Haploidentical or Unrelated Donor BMT to Restore Normal Hematopoiesis in Aplastic Anemia, Blood and Marrow Transplant Clinical Trials Network (BMT CTN) #2207
Authors: Akshay Sharma, Abhishek A. Mangaonkar, Adetola A. Kassim, Amber R. Fritz, Anna Bellach, Blachy J Davila Saldana, Brian J. Ball, Craig Malmberg, Daria V Babushok, Lori Henderson, Manu Pandey, Michael J Martens, Nancy DiFronzo, Nancy Geller, Nicole M. Ritzau, Sagar S. Patel, Srinivasa Reddy Sanikommu, Steven M. Devine, Steven Tsai, Larisa Broglie, Mary M. Horowitz, Sally Arai, Amy E. DeZern
Journal: Blood (2024)
Deep Learning-Driven 24-Hour Mortality Risk Assessment through Peripheral Blood Smear Morphology in Hospitalized Cancer Patients
Authors: Dylan C. Webb, Cesar Colorado-Jimenez, Maly Fenelus, Siddharth Singi, Zhanghan Yin, Sean Paulsen, K. Hasan Bilal, A. Zara Herskovitz, Samuel McCash, Linlin Wang, Mikhail Roshal, Lauren McVoy, Chad Vanderbilt, Ahmet Dogan, Gregory Mark Goldgof
Journal: Blood (2024)
A Clinical Overview of Clonal Cytopenia of Undetermined Significance in the Presence of <i>ZRSR2</i> Mutations
Authors: Mahmoud Yacout, Bahga Katamesh, Yazan Jabban, Rong He, Patricia Greipp, Dragan Jevremovic, James M. Foran, Cecilia Y. Arana Yi, Antoine N. Saliba, Abhishek A. Mangaonkar, Mithun V Shah, Mrinal M. Patnaik, Hassan B Alkhateeb, Aref Al-Kali
Journal: Blood (2024)
Phase 1 Trial of CD30-Directed, CCR4 Co-Expressing Chimeric Antigen Receptor T-Cells in Patients with CD30+ Cutaneous T-Cell Lymphomas Refractory to Brentuximab Vedotin
Authors: Daniel K Reef, Catherine Joyce Arago Cheng, Caroline Babinec, Kelly Hoye, John West, J. Kaitlin Morrison, Faith Brianne Buchanan, Ashley Zanter, Angela Denise Spruill, Kimberly A. Kasow, Anastasia Ivanova, Edith Bowers, Jonathan Serody, Barbara Savoldo, Gianpietro Dotti, Natalie Grover, Anne W Beaven
Journal: Blood (2024)
Single Cell Transcriptomics on Bone Marrow Biopsies Unveils Peculiar Bone Microenvironment Cell Subtypes and Highlights Alterations Correlated with High-Risk Features in Precursor Monoclonal Gammopathies and Multiple Myeloma Patients
Authors: Mattia Dessena, Tommaso Torelli, Cristina Manferdini, Denise Toscani, Alessandro Guidi, Rosanna Vescovini, Nicolas Thomas Iannozzi, Anna Benedetta Dalla Palma, Vincenzo Raimondi, Oxana Lungu, Federica Librale, Matia Bernardi, Stefania Ricci, Laura Pelagatti, Giannalisa Todaro, Gabriella Sammarelli, Camilla Sitzia, Emanuela Aleo, Gina Lisignoli, Luca Agnelli, Nicola Giuliani, Paola Storti
Journal: Blood (2024)
Trends and Disparities in Sickle Cell Disease-Related Mortality in the United States from 1999 to 2020: Insights from the CDC Wonder Database
Authors: Muhammad Kashif Amin, Umar Akram, Shahzaib Ahmed, Eeman Ahmad, Shoaib Ahmad, Fatima Tuz Zahra, Zeeshan Sattar, Muhammad Umair Mushtaq, Michael V. Jaglal, Moazzam Shahzad
Journal: Blood (2024)
A Multi-Site Break through Cancer Trial: Phase II Study Investigating Dual Inhibition of BCL2 and Menin in AML MRD Using the Combination of Venetoclax and Revumenib (Trial In Progress)
Authors: Ghayas C. Issa, Alexander J. Ambinder, Wenbin Xiao, Scott Manalis, Alex K Shalek, Lukasz P. Gondek, Alex Kentsis, Nicholas J. Short, Naval Daver, Jing Ning, Lianchun Xiao, Michael Hemann, Ken Chen, Keyur P. Patel, Pavan Bachireddy, Andrew A. Lane, Marina Konopleva, Omar Abdel-Wahab, Jeffrey J. Molldrem, Ross L Levine, Mark J. Levis, Richard M Stone, Michael Andreeff, Farhad Ravandi, Aaron D. Goldberg, Jacqueline S. Garcia
Journal: Blood (2024)
Long-Term Efficacy of Allogeneic Hematopoietic Stem Cell Transplantation for 532 Patients with KMT2A-Rearranged Acute Leukemia
Authors: Ruijuan Sun, Yue Lu, Jian-Ping Zhang, Jiarui Zhou, Deyan Liu, Yanli Zhao, Zhijie Wei, Min Xiong, Xingyu Cao, Peihua Lu
Journal: Blood (2024)
Omitting Ciprofloxacin Prophylaxis in Allogeneic Hematopoietic Stem Cell Transplantation Does Not Result in Inferior Outcomes
Authors: Krischan Braitsch, Vanessa Nehrbaß, Katharina Nickel, Maike Hefter, Katrin Koch, Kathrin Rothe, Florian Bassermann, Jochen Schneider, Katharina S. Götze, Peter Herhaus, Mareike Verbeek
Journal: Blood (2024)
BV-CHP in Previously Untreated Patients with CD30-Positive Adult T-Cell Leukemia-Lymphoma: A Multicenter Real-World Retrospective Study
Authors: Junya Makiyama, Masahito Tokunaga, Motoaki Shiratsuchi, Takanori Toyama, Satoshi Oka, Ilseung Choi, Takahiro Yoshida, Kiyoshi Okazuka, Atae Utsunomiya
Journal: Blood (2024)
A Randomized Phase II Study of Venetoclax and HMA-Based Therapies for the Treatment of Older and Unfit Adults with Newly Diagnosed FLT3-Mutated Acute Myeloid Leukemia (AML): A Myelomatch Treatment Trial: ECOG-ACRIN MM20A-EA02
Authors: Jessica Kaplan Altman, Zhuoxin Sun, Alexander E. Perl, Richard Little, Steven D. Gore, Laura C. Michaelis, Geoffrey L. Uy, Yasmin Abaza, Sameem Abedin, John L. Reagan, Ehab L. Atallah, Selina Luger, Mark R. Litzow
Journal: Blood (2024)
A Novel Oral Prodrug AN233 Induces Fetal Hemoglobin Expression in Sickle Cell Disease Mice and Baboons
Authors: Chithra D. Palani, Abraham Nudelman, Ada W. Rephaeli, Donald E. Lavelle, Manickam Alagar, Nikhil Patel, Zhi Wenbo, Betty S. Pace
Journal: Blood (2024)
Safety, Pharmacokinetics, Pharmacodynamics and Clinical Activity of KT-333, a Targeted Protein Degrader of STAT3, in Patients with Relapsed or Refractory Lymphomas, Leukemia, and Solid Tumors
Authors: Tatyana Feldman, Enrica Marchi, Stephen D. Smith, Adam J. Olszewski, Auris O Huen, Zachary D. Epstein-Peterson, Don A. Stevens, Alexander N. Starodub, Eric J. Feldman, Cristina P Rodriguez, John C. Reneau, Jonathan E. Brammer, Ahmad H. Mattour, Lauren C. Pinter-Brown, Rachelle Perea, Patrick Henrick, Joyoti Dey, Alyssa Fasciano, Rahul Karnik, Sagar Agarwal, Ashwin Gollerkeri, Jared Gollob, Aditi Shastri, Stefan K. Barta
Journal: Blood (2024)
Ultra-Sensitive <i>KIT</i> testing Uncovers Previously Undetected <i>KIT</i> mutations in Patients with Indolent Systemic Mastocytosis: Results from the Pioneer Trial
Authors: Deepti H. Radia, Tsewang Tashi, Ivan Alvarez-Twose, Patrizia Bonadonna, Hanneke Oude Elberink, Sonia Cerquozzi, Tracy I. George, Guang Yang, Mark Rosenzweig, Hui-Min Lin, Ben Lampson, Rachel L. Erlich, Jason Gotlib
Journal: Blood (2024)
Risk of Hematologic Malignancy Following Infectious Mononucleosis Caused By Epstein-Barr Virus: A Danish and Swedish Observational Study over 40 Years
Authors: Tine Kopp, Jonas Banefelt, Mathias Lilja, Susan Hall, Laura Hendrix, Sigrid DaVeiga, John Diaz-Decaro
Journal: Blood (2024)
Lower Respiratory Tract Pathogen Colonization Detected By Metagenomic Next-Generation Sequencing of Bronchoalveolar Lavage Fluid before Allogeneic Hematopoietic Stem Cell Transplantation and Its Predicting Value for Post-Transplant Infection
Authors: Hang Zhang, Hui Liu, Ting Liu, Ting Niu, Zhigang Liu, Jie Ji
Journal: Blood (2024)
Patient-Specific Platelet Phenotypes in Patients with Immune Thrombocytopenia
Authors: Sidra Ali, Sarah Hicks, Lucy Coupland, Simone Brysland, Vijay Bhoopalan, Jun Ng, Yee-Lin Thong, Samina Nazir, Robert K. Andrews, Elizabeth E. Gardiner, Philip Young-Ill Choi
Journal: Blood (2024)
Real-World Use Patterns and Clinical Outcomes for Myelodysplastic Syndrome Patients Initiating Oral Decitabine and Cedazuridine or Intravenous/Subcutaneous Hypomethylating Agents
Authors: Amer M. Zeidan, Ruizhi Zhao, Dudith Pierre-Victor, Yuexi Wang, Jon Tepsick, Ziyu Lan, Tehseen Salimi
Journal: Blood (2024)
Circulating Peripheral Blood Mononuclear Cells from Adults with Sickle Cell Disease (SCD)- Associated Pulmonary Hypertension (PH) Patients Have Increased Iron Content and a Unique Multi-Omic Signature
Authors: Christina Lisk, Francesca I Cendali, Delany Swindle, Gemlyn George, Rachelle Nuss, Kathryn Louise Hassell, Paul Buehler, Angelo D'Alessandro, David Irwin
Journal: Blood (2024)
Results from the Aurora Study: A Phase 2, Randomized, Double-Blind, Placebo-Controlled Study of Bitopertin in Erythropoietic Protoporphyria
Authors: Amy Dickey, Sioban Keel, Herbert L Bonkovsky, Karl Anderson, Manisha Balwani, Cynthia Levy, Manish Thapar, Bruce Wang, Brendan McGuire, Will Savage
Journal: Blood (2024)
Isatuximab, Pomalidomide, and Dexamethasone (IsaPd) As Salvage Therapy for Patients with Multiple Myeloma: Multicenter, Retrospective Clinical Experience with 262 Cases Outside of Controlled Clinical Trials
Authors: Enrica Antonia Martino, Daniele Derudas, Elena Rossi, Sofia Terlizzi, Giovanni Reddiconto, Paola Stefanoni, Jacopo Micozzi, Silvia Mangiacavalli, Elena Zamagni, Massimo Offidani, Anna Furlan, Gabriele Buda, Flavia Lotti, Carmine Liberatore, Antonio Lazzaro, Roberta Della Pepa, Giuseppe Bertuglia, Emiliano Barbieri, Concetta Conticello, Claudio De Magistris, Lorenzo De Paoli, Velia Bongarzoni, Anna Maria Cafro, Anna Mele, Pietro Benvenuti, Claudio Cerchione, Cirino Botta, Elisabetta Antonioli, Nicola Sgherza, Sara Aquino, Giuseppe Mele, Gregorio Barila, Salvatore Palmieri, Ombretta Annibali, Rosario Bianco, Massimiliano Arangio Febbo, Gloria Margiotta Casaluci, Angela Rago, Raffaele Fontana, Francesca Farina, Ernesto Vigna, Antonella Bruzzese, Catello Califano, Angela Amendola, Daniela Roccotelli, Alessandra Lombardo, Annalisa Citro, Giuseppina Uccello, Renato Zambello, Alessandro Maggi, Santo Neri, Michele Monachesi, Alessandro Gozzetti, Vittorio Montefusco, Marino Brunori, Nicola Di Renzo, Marta Coscia, Valerio De Stefano, Antonino Neri, Francesco Di Raimondo, Fortunato Morabito, Pellegrino Musto, Massimo Gentile
Journal: Blood (2024)
Trial in Progress: A Randomized-Controlled Phase 2 Study Evaluating Venetoclax Plus Azacitidine Versus Intensive Chemotherapy in Adult Patients with Newly Diagnosed, <i>NPM1</i>-Mutated AML - the SAL/AMLCG Vincent Trial
Authors: Lydia Kretschmer, Leo Ruhnke, Christoph Schliemann, Lars Fransecky, Björn Steffen, Martin Kaufmann, Andreas Burchert, Christoph Schmid, Maher Hanoun, Tim Sauer, Klaus H Metzeler, Kerstin Schäfer-Eckart, Mathias Hänel, Martina Crysandt, Paul Jäger, Stefan W. Krause, Christine Dierks, Stefan Klein, Nadia Maguire, Lukas Peter Frenzel, Veit L. Buecklein, Frank Fiebig, Anna Harig, Christian Thiede, Moritz Middeke, Richard Dillon, Claudia D Baldus, Hubert Serve, Uwe Platzbecker, Karsten Spiekermann, Wolfgang Hiddemann, Martin Bornhäuser, Richard F. Schlenk, Carsten Müller-Tidow, Christoph Röllig
Journal: Blood (2024)
Development of Induced Pluripotent Stem Cell-Derived T Cells Exhibiting Phenotypic and Functional Attributes of Primary CAR T Cells
Authors: Bryan Hancock, Jonatan Tuncel, Kyla Omilusik, Alison O'Connor, Bi-Huei Yang, Matthew Haynes, Amanda Yzaguirre, Karina Palomares, Sandeep Kothapally Hanok, Matthew Denholtz, Martin Hosking, Eigen Peralta, Tom Lee, Raedun Clarke, Sjoukje Van Der Stegen, John Goulding, Jode Goodridge, Michel Sadelain, Bahram Valamehr
Journal: Blood (2024)
Early Tapering of Immunosuppression in MRD Positive Myelofibrosis Patients Induces Molecular Response and Excellent Outcome after Hematopoietic Stem Cell Transplantation
Authors: Kristin Rathje, Kordelia Barbullushi, Nico Gagelmann, Anita Badbaran, Johanna Richter, Mathias Schäfersküpper, Franziska Elisabeth Marquard, Radwan Massoud, Sofia Oechsler, Evgeny Klyuchnikov, Ina Rudolph, Silke Heidenreich, Christian Niederwieser, Catherina Lück, Dietlinde Janson, Christine Wolschke, Boris Fehse, Francis A. Ayuk, Nicolaus Kroeger
Journal: Blood (2024)
Clinical Evaluation of Fast-in-Time (FIT) Anti-CD19 CAR T-a Non-Viral, 2-Day Rapid Manufacture CAR T-Cell Therapy for B-Cell Malignancies
Authors: Ping Li, Jian Ge, Shiguang Ye, Lili Zhou, Yiming Gong, Huaying Ruan, Hosein Kouros-Mehr, Aibin Liang
Journal: Blood (2024)
FLT3 Inhibitors As Maintenance Therapy Post Allogenic Hematopoietic Stem Cell Transplantation in Acute Myeloid Leukemia Patients with FLT3 Mutations; A Systematic Review and Meta-Analysis
Authors: Sadia Ansar, Mahnoor Asghar Keen, Mahnoor Sukaina, Muhammad Saeed, Zarlish Rehman, Roshaan Rehman, Qazi Muhammad Farooq Wahab, Faryal Masaud, Aqsa Mumtaz, Karan Jatwani, Muhammad Salman Faisal
Journal: Blood (2024)
Post-Injury Treatment with Rapid Intraosseous Injection of Lyophilized Synthetic Platelets Enhances Survival, Hemostasis, and Hemodynamics in a Rat Model of Liver Laceration
Authors: Zeyu Liu, Zachary A Secunda, Abiha Abdullah, Riya Sharma, Norman F Luc, Lauren Jackson, Baylee Traylor, Dante Disharoon, Christa Pawlowski, Ujjal Didar Singh Sekhon, Emma Quill, Philip Charles Spinella, Susan M Shea, Michael A Bruckman, Anirban Sen Gupta, Matthew Neal
Journal: Blood (2024)
Community Health Worker and Mobile Health Programs to Help Young Adults with Sickle Cell Disease Transition to Using Adult Healthcare Services – the Comets Study; Results from Patient-Reported Outcomes at 6 Months
Authors: Sophia Jan, Caren Steinway, Tanisha Belton, Justine Shults, Laura Bennett, Heather Griffis, Banu Aygun, Abena Appiah-Kubi, Nataly Apollonsky, Donna Boruchov, Omar Niss, Lisa A. Schwartz, Lori E. Crosby, Lamia Barakat, Biree Andemariam, David Rubin, Kim Smith-Whitley
Journal: Blood (2024)
Tumor-Primed CD3+CD56+ natural Killer T-like Cells As an Efficient Novel Cell Therapy for Relapsed/Refractory Multiple Myeloma
Authors: Ji Hyun Lee, Seok-Ho Kim, Junsang Doh, Duck Cho, Jeong-a Kim, Sung Yong Oh, Sung-Hyun Kim, Juheon Lee
Journal: Blood (2024)
Renew Trial in Progress: A Phase 3, Double-Blind, Placebo-Controlled Study to Evaluate the Efficacy and Safety of Elritercept (KER-050) for the Treatment of Transfusion-Dependent Anemia in Adult Participants with Very Low-, Low-, or Intermediate-Risk Myelodysplastic Neoplasms (MDS)
Authors: Rami S. Komrokji, Maria Diez-Campelo, Lynette C.Y. Chee, Thomas Cluzeau, Amy E. DeZern, Pierre Fenaux, Guillermo Garcia-Manero, Aristoteles Giagounidis, Uwe Platzbecker, Matteo Giovanni Della Porta, Valeria Santini, Mikkael A. Sekeres, Amer M. Zeidan, Rena Buckstein, Miranda Ross, Ying Jiang, Suresh Bobba, Montagu Hankin, Chris Materna, Christine Graham, Sanjay Thamake, Christopher Rovaldi, Dena Grayson, Jen L. Salstrom
Journal: Blood (2024)
A Phase Ia Study of VGA039, a Protein S-Targeting Monoclonal Antibody, in Individuals with Von Willebrand Disease Demonstrates Concentration-Dependent Increases in Thrombin Generation for Reducing Bleeding
Authors: Carolyn M Millar, Priyanka Raheja, Allison P Wheeler, Shrinath Kshirsagar, Christian Schoergenhofer, Nicoletta C Machin, Cihan Ay, Almudena Tercero, Hayley Lane, Christopher J Horvath, Sandip Panicker, Gary Patou, Benjamin Kim, Savita Rangarajan
Journal: Blood (2024)
Unmet Needs, Factor Consumption, and Healthcare Resource Use Among People with Hemophilia a: Real-World Analysis of the Adelphi Hemophilia Disease Specific ProgrammeTM
Authors: Lynn Malec, Davide Matino, Kieran Wynne-Cattanach, Chris Blazos, Duygu Bozkaya, Anne-Laure Tardy, Sylvie Bozzi, Jennifer Dumont
Journal: Blood (2024)
Loss of Negative Metabolic Feedback Drives <i>TET2</i> Mutant Inflammation
Authors: Geon Geon Kim, Christopher B. Hergott, Aidan P. Miller, Amy Deik, Meaghan Boileau, Kevin Bullock, Kerry Pierce, Angelina Choy, Wesley Shin, Marie E McConkey, Justin CT Loke, Birgitta Ryback, Michael N Trinh, Justine Rutter, Hong Yue, Paul Park, Shourya SR Burman, Eric Fischer, Scott A Armstrong, Clary Clish, Benjamin Levine Ebert
Journal: Blood (2024)
Predictors of Individual Symptom Scores in Myeloproliferative Neoplasms: A Real-World Retrospective Cohort Study
Authors: Muhammad Ali Khan, Syed Arsalan Naqvi, Cecilia Y. Arana Yi, John Camoriano, Joshua Blocher, Jennifer Andres, Irbaz Bin Riaz, Jeanne Palmer
Journal: Blood (2024)
Genome-Wide CRISPR/Cas9 Knockout Screen Reveals Novel LP-168 (Rocbrutinib) Combinations Targeting BCL-2 Protein Members for Chronic Lymphocytic Leukemia
Authors: Britten K. Gordon, Ethan C. Whipp, Lianbo Yu, Samon Benrashid, Andrew D. Mitchell, Alexander He, Jazmin Urrutia, Shrilekha Misra, Alexander R. Marr, Tzung-Huei Lai, Naina Karnati, Shanmugapriya Thangavadivel, Kerry A. Rogers, Seema A. Bhat, Nicole R. Grieselhuber, Yi Chen, Fenlai Tan, Stephen P. Anthony, Yu Chen, Deepa Sampath, Rosa Lapalombella, Jennifer A. Woyach
Journal: Blood (2024)
PIM447, a Pan-PIM Kinase Inhibitor, in Combination with Venetoclax Exerts a Potent Anti-Tumor Activity in the Bone Marrow Niche
Authors: Fernanda Marconi Roversi, Maura Lima Pereira Bueno, Samara de Sousa Mariano, Fernanda Soares Niemann, Adriana da Silva Santos Duarte, Audrey Bastos, Nádia Ghinelli Amôr, Irene Santos, Jose Andres Yunes, Sandra Pinho, Sara Teresinha Olalla Saad
Journal: Blood (2024)
Pain Reduction Following Treatment of Bleeding Episodes with Eptacog Beta in Adults and Adolescents with Hemophilia A or B Complicated By Inhibitors
Authors: Tyler W. Buckner, Craig Kessler, Giancarlo Castaman, Cédric Hermans, Victor Jimenez-Yuste, Johnny Mahlangu, Wolfgang A. Miesbach, Johannes Oldenburg, Michael Recht, Leonard A. Valentino, Allison P Wheeler, Steven W. Pipe
Journal: Blood (2024)
Expanding the Eureka Study: Integrating a Comprehensive Clinical Registry with Molecular Profiling to Advance AL Amyloidosis Research
Authors: Mario Nuvolone, Ute Hegenbart, Bruno Paiva, Monique C. Minnema, Enkelejda Miho, Marta Lasa, Paolo Milani, Alain van Mil, Marish I. F. Oerlemans, Jan Kruta, Ramon Lecumberri Villamediana, Alice Nevone, Luca Arcaini, Francesca Gay, Francesco Di Raimondo, Pellegrino Musto, Eloisa Riva, Mohammed Aljama, Krzysztof Jamroziak, Roberta Shcolnik Szor, Mathias Brehon, Giampaolo Merlini, Stefan Schonland, Giovanni O. Palladini
Journal: Blood (2024)
Prophylactic Administration of Glucocorticoids and Tacrolimus in AAV8-F8 Gene Therapy of Severe Haemophilia-a Achieved a Significant Long-Term Efficacy
Authors: Wei Liu, Xiaolei Pei, Bingqi Xu, Xinyue Dai, Feng Xue, Linging Chen, Yuhua Wang, Yunfei Chen, Xiaofan Liu, Rongfeng Fu, Wentian Wang, Ying Chi, Huiyuan Li, Renchi Yang, Lei Zhang
Journal: Blood (2024)
Lymphocyte Dynamics during the Treatment of SR-aGVHD with Mesenchymal Stem Cells Derived from Human Umbilical Cord Blood - a Phase III, Multi-Center, Prospective, Single-Arm Pivotal Study
Authors: Sheng Chen, Dongxue Ge, Kun Qian, Jingwen Tang, Yujun Wei, Liping Dou, Daihong Liu
Journal: Blood (2024)
Real-World Effectiveness of Ravulizumab Among Adults with Atypical Hemolytic Uremic Syndrome (aHUS) Who Switched to Ravulizumab within 3 Months of Eculizumab Treatment: A Physician Panel-Based Chart Review Study (aHUS IMPACT)
Authors: Shruti Chaturvedi, Yan Wang, Moh-Lim Ong, Arpita Nag, Rui Song, Lynn Huynh, Jordan A. Burdeau, Mei Sheng Duh, Ramy Magdy Hanna
Journal: Blood (2024)
A Single-Cell T-Cell Reference Map Delineates the Biological Landscape of CD4+ T Cells in Myelodysplastic Syndromes Under Venetoclax Therapy
Authors: Juan Jose Rodriguez Sevilla, Yang Liu, Irene Ganan-Gomez, Vera Adema, Kelly S. Chien, Guillermo Montalban-Bravo, Natthakan Thongon, Guillermo Garcia-Manero, Rashmi Kanagal-Shamanna, Sanam Loghavi, Hui Yang, Linghua Wang, Simona Colla
Journal: Blood (2024)
Invasive Fungal Disease in Patients Undergoing Allogeneic Hematopoietic Stem Cell Transplantation in China: A Multicenter Epidemiological Study (CAESAR 2.0)
Authors: Chuan Li, Danping Zhu, Jia Chen, Xiaoyu Zhu, Nainong Li, Weijie Cao, Zhongming Zhang, Yehui Tan, Xiaoxia Hu, Hailong Yuan, Xiaosheng Fang, Yue Yin, Hongtao Wang, Nan Li, Xiao Jun Huang, Yuqian Sun
Journal: Blood (2024)
Mosaic Chromosomal Alterations Driving Clonal Hematopoiesis Show Shared and Divergent Patterns of Accumulation Among Humans of Diverse Ancestries
Authors: Jasmine Ryu Won Kang, June Kim, Kimberly Skead, Vanessa Bruat, Michelle Harwood, David Soave, Quaid D. Morris, Marie-Julie Fave, Philip Awadalla
Journal: Blood (2024)