Conditions: Gaucher Disease
Keywords: Gaucher disease pediatrics
Allocation: NON_RANDOMIZED | Intervention model: PARALLEL
Enrollment: 15
Healthy volunteers: no

Brief summary:
A protocol to extend the assessment of the safety and efficacy of taliglucerase alfa in pediatric subjects (2 to \<18 years old) with symptoms and clinical manifestations of Gaucher disease who completed treatment in Protocols PB-06-002 (switchover study from imiglucerase) or PB-06-005 (naïve treatment with taliglucerase alfa).

Detailed description:

Arms:
arm 1: None arm 2: None

Interventions: intervention 1: Taliglucerase alfa
Intervention descriptions: intervention 1: Taliglucerase alfa for infusion every two weeks for 24 months

Protocol document: