Conditions: Muscular Dystrophies
Keywords: Duchenne Muscular Dystrophy DMD 968 GSK Duchenne
Allocation: RANDOMIZED | Intervention model: SINGLE_GROUP
Enrollment: 186
Healthy volunteers: no

Brief summary:
The purpose of this study is to determine whether GSK2402968 is effective in the treatment of ambulant boys with Duchenne muscular dystrophy resulting from a mutation thought to be corrected by exon 51 skipping.

Detailed description:

Arms:
arm 1: 6mg/kg arm 2: dose-matched

Interventions: intervention 1: GSK2402968 6mg/kg/week
Intervention descriptions: intervention 1: subcutaneous

Protocol document: