Conditions: Iron Overload Due to Repeated Red Blood Cell Transfusions
Allocation: NA | Intervention model: SINGLE_GROUP
Enrollment: 32
Healthy volunteers: no

Brief summary:
The purpose of this study is to evaluate SSP-004184AQ in patients with transfusional iron overload whose primary diagnosis is hereditary or congenital anemia.

SSP-004184AQ is an iron chelator under development for chronic daily oral administration to patients with transfusional iron overload.

Detailed description:

Arms:
arm 1: 50 mg/kg/day orally twice daily for 24 weeks

Interventions: intervention 1: SPD602
Intervention descriptions: intervention 1: 50 mg/kg/day orally twice daily for 24 weeks

Protocol document: