Conditions: Mucopolysaccharidosis VI
Allocation: NON_RANDOMIZED | Intervention model: SINGLE_GROUP
Enrollment: 39
Healthy volunteers: no

Brief summary:
The purpose of this study is to evaluate the long-term efficacy and safety of rhASB treatment in patients with Mucopolysaccharidosis VI.

Detailed description:

Arms:
arm 1: N-acetylgalactosamine 4-sulfatase arm 2: None

Interventions: intervention 1: N-acetylgalactosamine 4-sulfatase intervention 2: Placebo/rhASB
Intervention descriptions: intervention 1: None intervention 2: None

Protocol document: