AAV GENE THERAPY We are a global leader in developing gene therapies that have the potential to transform the way diseases are treated. LEARN MORE POWERING A NEW FIELD OF DISCOVERY REGENXBIO is seeking to improve lives through the curative potential of gene therapy. Our NAV® Technology Platform has ushered in a new era of gene therapy innovation. LEARN MORE THERAPEUTIC PROGRAMS RETINAL DISEASES NEURODEGENERATIVE DISEASES METABOLIC DISEASES LEARN MORE PATIENTS & FAMILIES We are deeply committed to discovering and developing innovative gene therapies to improve treatment options for people with severe and debilitating diseases with significant unmet needs. Gene Therapy | Wet AMD | DMD | MPS II | MPS I | CLN2 | Expanded Access LEARN MORE PARTNERS & LICENSEES Partnerships and licensing are a key part of REGENXBIO’s commitment to enabling the ongoing development of gene therapy treatments using our NAV Technology Platform. LEARN MORE WHAT WE DO REGENXBIO is a leading clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy. Our gene therapy product candidates are designed to deliver genes to cells to address genetic defects or to enable cells in the body to produce therapeutic proteins that are intended to impact disease. Through a single administration, our gene therapy product candidates are designed to provide long-lasting effects, potentially significantly altering the course of disease and delivering improved patient outcomes. LEARN MORE LATEST REGENXBIO Announces Orphan Drug Designation Granted To RGX-202, A Novel Gene Therapy Candidate For The Treatment Of Duchenne Muscular Dystrophy REGENXBIO Inc. News Releases November 22, 2021 REGENXBIO Presents Additional Positive Interim Data From Trials Of RGX-314 In Wet AMD And Diabetic Retinopathy Using Suprachoroidal Delivery At AAO 2021 REGENXBIO Inc. News Releases November 12, 2021 REGENXBIO Announces Closing Of Eye Care Collaboration Agreement With AbbVie REGENXBIO Inc. News Releases November 9, 2021 READ MORE SIGN UP Receive updates to stay connected on REGENXBIO programs and our commitment to patients. Subscribe CONTACT US 9804 Medical Center Drive, Rockville, MD 20850 240.552.8181 General Info | Medical Info | Patient Advocacy | Partners | Investors | Media FOLLOW US ©2021 REGENXBIO Inc. "NAV®" is a registered trademark of REGENXBIO Inc. All rights reserved. Privacy Policy | Terms and Conditions