SUBSCRIBE Genetics 20 hours ago Genetic Variant Discovered in Amish Protects from Heart Disease Researchers link a missense mutation in the B4GALT1 gene to lower levels of LDL cholesterol and the blood clotting factor fibrinogen. 2 days ago In Editing RNA, Researchers See Endless Possibilities Technique Talk: CRISPR for Genome Engineering in Drosophila The Scientist Speaks - Molecular Farming: The Future of Pharmaceuticals HomeCategoriesGenetics Doctors Treat Girl’s Genetic Disorder with Repurposed Drug Amanda Heidt | Dec 1, 2021 In just 16 months, physicians went from identifying a novel rare disease in three-year-old Marley to successfully treating her with a drug previously used to treat African sleeping sickness and pediatric cancer. 2021 Top 10 Innovations The Scientist Staff | Dec 1, 2021 The COVID-19 pandemic is still with us. Biomedical innovation has rallied to address that pressing concern while continuing to tackle broader research challenges. Page 1 of 41 123456789 Trending Moderna vs. Pfizer: Is There a “Best” mRNA Vaccine? Omicron Is WHO’s Fifth Variant of Concern, Experts Urge Patience 2021 Top 10 Innovations Over the Counter Antihistamines Could Help Against Cancer Multimedia December 2021 Interactive Crossword Infographic: How Worms that Reside in the Gut Could Influence Health DECEMBER 2021 Return of the worms Researchers are carefully considering the therapeutic potential of helminths SUBSCRIBE TODAY Return of the Worms Immunologists and parasitologists are working to revive the idea that helminths, and more specifically the molecules they secrete, could help treat allergies and autoimmune disease. 2021 Top 10 Innovations The COVID-19 pandemic is still with us. Biomedical innovation has rallied to address that pressing concern while continuing to tackle broader research challenges. Sponsored ContentLabQuizzesWebinarsVideosInfographicseBooks Sponsored Interactive Crossword Puzzle Focus on Structure to Verify Protein Function Scientists analyze a therapeutic protein’s secondary structure to confirm drug efficacy and safety. Technique Talk: CRISPR for Genome Engineering in Drosophila Discover how CRISPR is revolutionizing gene editing in a classic genetics research model. A Library at Your Fingertips Scientists explore big questions and expand their knowledge with digital books. MarketplaceSponsored Product Updates An Early Start: The Impact of the Microbiome on Pediatric Development in the First Year of Life A better understanding of early childhood microbiome shifts offers a unique window for detecting disease risk and intervening appropriately. Dr. Aletta Schnitzler Joins TurtleTree as Chief Scientific Officer Cell-based nutrition company TurtleTree welcomes Dr. Aletta Schnitzler as its new Chief Scientific Officer (CSO). With her world-class expertise in cellular bioprocessing, Dr. Schnitzler’s appointment marks a significant stride in TurtleTree’s journey towards sustainable and efficient cellular food production. Streamlining Quality Control for Cultured Human Cells Guidelines for maintaining human cells grown ex vivo Understanding Cytokine Release Syndrome in COVID-19 Patients Researchers detect aberrant cytokine activity in response to SARS-CoV-2 infection. Stay Connected with E-NEWSLETTER SIGN-UP Subscribe to receive The Scientist Daily E-Newsletter in your inbox! 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