Careers Contact Us Facebook Twitter LinkedIn Home About Science Clinical Trials Patients & Families Investors & Media Sanfilippo Syndrome Type A (MPS IIIA) OVERVIEW RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA (RDEB) SANFILIPPO SYNDROME TYPE A (MPS IIIA) SANFILIPPO SYNDROME TYPE B (MPS IIIB) An open-label, dose-escalation clinical trial assessing the safety of one-time gene therapy ABO-102 for younger, higher-functioning patients with MPS IIIA. VIEW STUDY An open-label clinical trial assessing the safety of one-time gene therapy ABO-102 for patients with middle and advanced phases of MPS IIIA. VIEW STUDY © 2021 Abeona Therapeutics Inc. All Rights Reserved. | Privacy Policy