About Gene Therapy Investors & Newsroom Patients Healthcare Professionals Careers & Contact Company Profile: Delivering on the promise of gene therapy. Home About Our focus is to advance the future of medicine through gene therapy. We have the resources and experience to achieve this. uniQure is delivering on the promise of gene therapy, single treatments with potentially curative results. We have developed a modular technology platform to rapidly bring new disease-modifying therapies to patients with severe genetic diseases. We are advancing a focused pipeline of innovative gene therapies and have established clinical proof-of-concept in our lead indication, hemophilia B, and preclinical proof-of-concept in Huntington’s disease. Our pipeline of adeno-associated virus (AAV)-based gene therapies has been developed using an innovative technology platform, supported by industry-leading proprietary commercial-grade manufacturing capabilities. Through recent collaborations and our strategic partnership with Bristol-Myers Squibb to develop gene therapies for cardiovascular diseases, we have taken the next steps toward developing gene therapies targeting chronic and degenerative diseases that affect larger populations. uniQure’s state-of-the-art manufacturing facility in Lexington, Mass. complements research and development in Amsterdam, the Netherlands and Heidelberg, Germany. Learn more about our work to deliver curative gene therapies that transform the lives of patients. IN THIS SECTION: > Company Profile > Mission, Vision & Values > Management Team > Board of Directors > Our Locations > Partners > Photo Gallery uniQure N.V. Paasheuvelweg 25a, 1105 BP, Amsterdam Chamber of Commerce 33301321 QUICK LINKS Patients Careers Locations Glossary CONTACT US! info@uniQure patients@uniQure investors@uniQure media@uniQure Sitemap | Disclaimer | Privacy Statement About Gene Therapy Investors & Newsroom Patients Healthcare Professionals Careers & Contact

About Gene Therapy Investors & Newsroom Patients Healthcare Professionals Careers & Contact About: Mission, Vision & Values Home About “Our mission at uniQure is to deliver curative gene therapies that transform the lives of patients.” Vision “Our vision at uniQure is to build an industry-leading, fully integrated and global company that leverages its validated technology and manufacturing platform to deliver transformative gene therapy products to patients with serious unmet medical needs.” Values Be passionate about the patient. Act with integrity and respect. Take ownership and act with urgency. Collaborate for success. Innovate every day. We value our team and what we can achieve together. uniQure N.V. Paasheuvelweg 25a, 1105 BP, Amsterdam Chamber of Commerce 33301321 QUICK LINKS Patients Careers Locations Glossary CONTACT US! info@uniQure patients@uniQure investors@uniQure media@uniQure Sitemap | Disclaimer | Privacy Statement About Gene Therapy Investors & Newsroom Patients Healthcare Professionals Careers & Contact