Title: Orphan
Description: "This book is about the struggle to save the lives of children who, because of a roll of the genetic dice, are born with any one of more than several thousand rare genetic disorders. It recounts the now century long effort of small groups of physicians and scientists to take on some of these genetic diseases. In many cases just a few physician-scientists have made an immense contribution to blazing a path toward new therapies"--
Subjects: Research, Genetic disorders in children, Medical genetics, Genetic disorders, Inborn Genetic Diseases, Child, Rare Diseases, SCIENCE / Life Sciences / Genetics & Genomics, MEDICAL / Diseases, MEDICAL / Pediatrics