Manufacturing of Gene Therapeutics - Methods, Processing, Regulation and Validation
Edition: 1 edition
Publisher: Springer
Published: December 1, 2001
Language: eng
Format: Hardcover
Number of pages: 345
ISBN-13: 9780306466809
Subjects: Medical genetics; Pharmaceutical technology; Biotechnology (General); Genetics; Science; Medical; Biotechnology; Life Sciences - Genetics & Genomics; Genetic Engineering; Medical / Pharmacy; Medical : Biotechnology; Science / Biotechnology; Science : Life Sciences - Genetics & Genomics; Drug Approval; Gene Therapy; Genetic transformation; Genetic vectors
First sentence: Gene therapy may be defined as the introduction of genetic material into the cells of a patient in an effort to help cure the disease either by producing a gene product which is missing or in reduced amounts in the patient due to a genetic mutation in the individual (eg Factor VIII protein for haemophilia) or by introduction of new genetic material which either directly or indirectly will help to combat the disease (eg genetic vaccination).