Retinal Dystrophies
Subtitle: Functional Genomics to Gene Therapy (Novartis Foundation Symposia)
Publisher: Wiley
Published: January 26, 2004
Language: eng
Number of pages: 226
ISBN-13: 9780470853573
First sentence: The road from gene discovery to gene therapy for inherited retinal diseases has taken an interesting path.
Description: Covers all aspects of retinal dystrophies from the molecular and developmental biology of these disorders to possible therapeutic approaches, with special reference to gene therapy. Specific chapters deal with the molecular genetics of gene therapies, clinical genetic studies, molecular and cellular mechanisms of the development of the disease, functional genomics of retinal diseases, animal models of retinal dystrophies and studies on gene therapy approaches to correcting the disorder.