The slightly elevated temperature then stops the leakage of blood vessels and reduces the size of lesions in that area. Although preliminary studies are promising, further research is needed to refine this process. The vehicle for delivering genes or genetic information into the nucleus of a cell. Vectors act like a fleet of microscopic delivery trucks transporting new, therapeutic genes into retinal cells. Most vectors are modified forms of viruses.
Viruses are extremely effective at getting inside a cell.
However, viruses also contain elements that may damage cells. Over the past decade, researchers have been working to genetically modify viruses to be safe and have few immune side effects, without compromising their delivery capabilities. Importantly, the X- chromosome also contains many other genes that have nothing to do with determination of gender. These are called X-linked diseases. Females can be carriers of the mutated genes but seldom show signs of the disease since they bear another X chromosome that does not have the same mutation and thus produces a normal protein.