Potential Areas of Application Knowledge of the gene and its sequence and structure may allow diagnosis of any associated familial disorders. Delivery of the gene to specific tissues could correct tissue-specific defects. Delivery to liver may affect whole body glucose metabolism. Gene or its expression product could serve as a potential target for drug screening. The human gene and cDNAs are cloned and the gene structure is known.
Efforts are in progress to clone animal versions so that trials on animal models can be initiated.
For certain technologies, information not publicly available can be obtained with a signed confidentiality agreement that must be received by this office.