TrialPanorama/TrialPanorama-database huggingface dataset:
Primary endpoint: HOOS preoperative activity of daily living scores
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: NoGo error rate
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: NoGo N2 amplitude
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: FOI achievement rate
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Mean time to successful intubation on the first attempt
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: rate of treatment compliance
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Pain scores during catheter insertion
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: cost-effectiveness of supervised treatment
Endpoint domain: Resource use
Endpoint subdomain: Other resource use
Primary endpoint: Vegetable intake improvement
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Healthcare providers' awareness of PCC-risk factors
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: Healthcare providers' competence in discussing PCC
Endpoint domain: Life impact
Endpoint subdomain: Delivery of care
Primary endpoint: scoliotic angle
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: ICD-shocks
Endpoint domain: Physiological/clinical
Endpoint subdomain: Cardiovascular outcomes
Primary endpoint: urinary 2‐OHE1:16α‐OHE1 ratio
Endpoint domain: Physiological/clinical
Endpoint subdomain: Neoplasms and related outcomes
Primary endpoint: Fasting blood sugar concentration
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: Frequency of 24-hour premature ventricular beats
Endpoint domain: Physiological/clinical
Endpoint subdomain: Cardiovascular outcomes
Primary endpoint: Quiz score improvements
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Improvements in awareness of AD risk reduction strategies
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: Willingness to volunteer for AD causes
Endpoint domain: Life impact
Endpoint subdomain: Role functioning
Primary endpoint: 28-day cumulative incidence of mortality
Endpoint domain: Mortality/survival
Primary endpoint: Reduced use of antipseudomonal and anti-MRSA agents
Endpoint domain: Resource use
Endpoint subdomain: Need for further intervention
Primary endpoint: DIAGNOdent reading of WSLs
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: 24-hour seizure rate
Endpoint domain: Physiological/clinical
Endpoint subdomain: Nervous system outcomes
Primary endpoint: Non-rapid eye movement stage 2 sleep duration
Endpoint domain: Life impact
Endpoint subdomain: Sleep
Primary endpoint: Yo-Yo Intermittent Recovery Test Level 1 distance
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Reduction of UL symptoms
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Improvement in patient-reported outcomes scores
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: Time to drainage removal
Endpoint domain: Physiological/clinical
Endpoint subdomain: Surgical and medical procedures outcomes
Primary endpoint: Public stigma
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: Serum MTL concentrations
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Contraceptive prevalence among adolescents
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Reduction in median birthweight centiles
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Glycemic control (reduction in fasting and post-prandial glucose)
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: axial diffusivity
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: radial diffusivity
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: mean trustworthiness ratings
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: Increase in brain injury biomarkers
Endpoint domain: Physiological/clinical
Endpoint subdomain: Nervous system outcomes
Primary endpoint: PERFECT scheme score
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: maternal composite outcome
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Peripheral insulin sensitivity (M value)
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: HOMA insulin resistance index (HOMA-IR)
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: Incidence of PUs of category 2 or worse
Endpoint domain: Physiological/clinical
Endpoint subdomain: Skin and subcutaneous tissue outcomes
Primary endpoint: Incidence of sacral PUs
Endpoint domain: Physiological/clinical
Endpoint subdomain: Skin and subcutaneous tissue outcomes
Primary endpoint: Incidence of innocent AAA
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Symptoms associated with Group 1 (high pitch strain while singing)
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Symptoms associated with Group 1 (unilateral throat pain)
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Use of the most effective methods of contraception
Endpoint domain: Physiological/clinical
Endpoint subdomain: Reproductive system and breast outcomes
Primary endpoint: Blood CD34+ cell counts
Endpoint domain: Physiological/clinical
Endpoint subdomain: Blood and lymphatic system outcomes
Primary endpoint: Collection yield of the first apheresis
Endpoint domain: Physiological/clinical
Endpoint subdomain: Blood and lymphatic system outcomes
Primary endpoint: Total yield of CD34+ cells
Endpoint domain: Physiological/clinical
Endpoint subdomain: Blood and lymphatic system outcomes
Primary endpoint: C index for CSS prediction
Endpoint domain: Mortality/survival
Primary endpoint: Myocardial Infarction Admission
Endpoint domain: Physiological/clinical
Endpoint subdomain: Cardiovascular outcomes
Primary endpoint: Stroke Admission
Endpoint domain: Physiological/clinical
Endpoint subdomain: Cardiovascular outcomes
Primary endpoint: HEI-2010 total score
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Overall rate of clinical improvement on day 28
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Time to virus nucleic acid negative conversion
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Abundance of polyunsaturated fatty acids (PUFA)
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Unsaturated fatty acids/saturated fatty acids ratio
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: FADS1 gene expression
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Mean concentration of semen
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Total motility of sperm
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Progressive motility of sperm
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: seroconversion rate of anti-EV71
Endpoint domain: Physiological/clinical
Endpoint subdomain: Immune system outcomes
Primary endpoint: geometric mean titer of anti-EV71
Endpoint domain: Physiological/clinical
Endpoint subdomain: Immune system outcomes
Primary endpoint: self-report self-esteem
Endpoint domain: Life impact
Endpoint subdomain: Emotional functioning/wellbeing
Primary endpoint: eating disorder psychopathology measure
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Increase in fatty acids (FAs) levels
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: Mortality due to bleeding
Endpoint domain: Mortality/survival
Primary endpoint: Mortality due to myocardial infarction (MI)
Endpoint domain: Mortality/survival
Primary endpoint: Adequate titre response after treatment
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Improvement in academic scores
Endpoint domain: Life impact
Endpoint subdomain: Cognitive functioning
Primary endpoint: Inflammatory cytokine levels in rectal mucosa
Endpoint domain: Physiological/clinical
Endpoint subdomain: Immune system outcomes
Primary endpoint: Postoperative QoR scores
Endpoint domain: Life impact
Endpoint subdomain: Global quality of life
Primary endpoint: shorter procedure time
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: shorter total radiofrequency application time
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: radiofrequency time per application
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Engagement in ECD-related activities
Endpoint domain: Life impact
Endpoint subdomain: Cognitive functioning
Primary endpoint: TFV-DP concentration in PBMC
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Unqualified success rate
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Mean level of Na reported on nutrient labels
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: abdominal pain intensity
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Technical skill score
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Non-technical skill score
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: LCQ improvement
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: FACIT score improvement
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: Dynamic and static balance
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: hemorrhage volume
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Cumulative retention failure
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Freedom from heart failure hospitalization
Endpoint domain: Mortality/survival
Primary endpoint: Mean CK-MB levels after 8 hours
Endpoint domain: Physiological/clinical
Endpoint subdomain: Cardiovascular outcomes
Primary endpoint: Mean CK-MB levels after 24 hours
Endpoint domain: Physiological/clinical
Endpoint subdomain: Cardiovascular outcomes
Primary endpoint: Quality of life in epilepsy scores
Endpoint domain: Life impact
Endpoint subdomain: Global quality of life
Primary endpoint: Incidence of severe ARD
Endpoint domain: Adverse events/effects
Primary endpoint: impaired global clustering coefficient
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Ankle joint position sense
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Post-transplant immune medication-free remission
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Ambulation without assistance
Endpoint domain: Life impact
Endpoint subdomain: Physical functioning
Primary endpoint: Risk of readmission due to AHF
Endpoint domain: Mortality/survival
Primary endpoint: lower risk of adverse kidney outcomes
Endpoint domain: Mortality/survival
Primary endpoint: bacteria recovery
Endpoint domain: Physiological/clinical
Endpoint subdomain: Infections and infestations outcomes
Primary endpoint: Modern contraceptive use
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Covert contraceptive use
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Decrease in salivary Streptococcus mutans and Lactobacillus
Endpoint domain: Physiological/clinical
Endpoint subdomain: Immune system outcomes
Primary endpoint: Median scores post intervention
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Ease of performing self-sampling
Endpoint domain: Life impact
Endpoint subdomain: Physical functioning
Primary endpoint: Cognitive capacity (MoCA)
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: prevalence of cardiometabolic risk factors
Endpoint domain: Physiological/clinical
Endpoint subdomain: Cardiovascular outcomes
Primary endpoint: Improvement in size of infantile hemangioma (IH)
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Improvement in color of infantile hemangioma (IH)
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Coefficient of involution
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: annualised risk of death
Endpoint domain: Mortality/survival
Primary endpoint: Percentage of patients with at least one error
Endpoint domain: Adverse events/effects
Primary endpoint: Error rate in ePRO vs P&P assessments
Endpoint domain: Adverse events/effects
Primary endpoint: time for dressing changes
Endpoint domain: Resource use
Endpoint subdomain: Other resource use
Primary endpoint: time for wound-related procedures
Endpoint domain: Resource use
Endpoint subdomain: Other resource use
Primary endpoint: Cervical Range of Motion (ROM)
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: mean VA over 24 weeks
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: time to clearance of vitreous hemorrhage
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Bone uptake
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Net bone volume
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: acute eGFR slope
Endpoint domain: Physiological/clinical
Endpoint subdomain: Renal and urinary outcomes
Primary endpoint: Change in ALBI score
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: BPDSI change
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: POCE (Primary Outcome Composite Endpoint)
Endpoint domain: Mortality/survival
Primary endpoint: DOCE (Definite or Probable Cardiac Events)
Endpoint domain: Mortality/survival
Primary endpoint: Alarm fatigue scores
Endpoint domain: Life impact
Endpoint subdomain: Emotional functioning/wellbeing
Primary endpoint: Total number of alarms
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Nonactionable alarms
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Opsonophagocytic activity (OPA) geometric mean titers (GMTs)
Endpoint domain: Physiological/clinical
Endpoint subdomain: Immune system outcomes
Primary endpoint: Progression-free median survival time
Endpoint domain: Mortality/survival
Primary endpoint: Mean DI
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Soil pH
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Fungal population
Endpoint domain: Physiological/clinical
Endpoint subdomain: Immune system outcomes
Primary endpoint: Bacterial population
Endpoint domain: Physiological/clinical
Endpoint subdomain: Immune system outcomes
Primary endpoint: Reduction of individual embitterment
Endpoint domain: Life impact
Endpoint subdomain: Emotional functioning/wellbeing
Primary endpoint: Reduction in intracranial pressure (ICP)
Endpoint domain: Physiological/clinical
Endpoint subdomain: Neurological outcomes
Primary endpoint: 28-day transplant-free survival
Endpoint domain: Mortality/survival
Primary endpoint: New onset acute kidney injury
Endpoint domain: Adverse events/effects
Primary endpoint: complete tumor response
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: remission from PND
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Duration of abnormal movement
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Postprandial adiponectin response
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: Postprandial FGF21 concentrations
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: Mortality and chronic complications
Endpoint domain: Mortality/survival
Primary endpoint: 2-h postprandial blood glucose
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: QALD by EQ‐5D‐5L
Endpoint domain: Life impact
Endpoint subdomain: Global quality of life
Primary endpoint: exercise capacity (VO2peak)
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: health-related quality of life (physical function)
Endpoint domain: Life impact
Endpoint subdomain: Physical functioning
Primary endpoint: Median number of steps per day
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Weight change difference
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: MedDiet score change
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: body image and sense of well-being
Endpoint domain: Life impact
Endpoint subdomain: Emotional functioning/wellbeing
Primary endpoint: Rate of Grade A screws placement
Endpoint domain: Physiological/clinical
Endpoint subdomain: Surgical and medical procedures outcomes
Primary endpoint: micro-leakage of crowns cemented with resin modified glass cement
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: FSFI score improvement
Endpoint domain: Life impact
Endpoint subdomain: Sexual functioning
Primary endpoint: worse asthma control
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: CNS Vital Signs Neurocognitive Index
Endpoint domain: Physiological/clinical
Endpoint subdomain: Nervous system outcomes
Primary endpoint: Alzheimer's Questionnaire Change score
Endpoint domain: Life impact
Endpoint subdomain: Cognitive functioning
Primary endpoint: Cognitive Functioning (CFQ)
Endpoint domain: Life impact
Endpoint subdomain: Cognitive functioning
Primary endpoint: Overall MyCQ score
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: Level of fear
Endpoint domain: Life impact
Endpoint subdomain: Emotional functioning/wellbeing
Primary endpoint: mean power
Endpoint domain: Physiological/clinical
Endpoint subdomain: Musculoskeletal and connective tissue outcomes
Primary endpoint: improvement in perceived life satisfaction
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: Complete response rates for vomiting
Endpoint domain: Physiological/clinical
Endpoint subdomain: Gastrointestinal outcomes
Primary endpoint: Complete response rates for nausea
Endpoint domain: Physiological/clinical
Endpoint subdomain: Gastrointestinal outcomes
Primary endpoint: Mean nausea score
Endpoint domain: Physiological/clinical
Endpoint subdomain: Gastrointestinal outcomes
Primary endpoint: comprehension assessment scores
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: recall assessment scores
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: time spent on the document
Endpoint domain: Life impact
Endpoint subdomain: Cognitive functioning
Primary endpoint: Relative expression levels of miR-146a and miR-9
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Superoxide dismutase levels
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Faster healing of wounds
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Preventing cardio-respiratory hospitalizations
Endpoint domain: Physiological/clinical
Endpoint subdomain: Respiratory outcomes
Primary endpoint: Intraoperative glucose levels
Endpoint domain: Physiological/clinical
Endpoint subdomain: Metabolic and nutritional outcomes
Primary endpoint: Consonant proficiency (PCC score)
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Proportion of participants with primary VPC
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Decreased displacement
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Mean scores of teachers' knowledge and attitude
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: Change in pupil diameter from baseline
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Percentage of eyes returning to baseline pupil diameter
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Percentage of eyes returning to baseline accommodative amplitude
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Symptoms of anxiety disorders
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Quality of life - psychological health
Endpoint domain: Life impact
Endpoint subdomain: Global quality of life
Primary endpoint: Risk of early recurrences
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: major bleeding risk
Endpoint domain: Adverse events/effects
Primary endpoint: ischemic risk
Endpoint domain: Physiological/clinical
Endpoint subdomain: Cardiovascular outcomes
Primary endpoint: LN metastasis prediction
Endpoint domain: Physiological/clinical
Endpoint subdomain: Neoplasms and related outcomes
Primary endpoint: Symptom medication score
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Incidence of second primary lung cancer
Endpoint domain: Mortality/survival
Primary endpoint: walking efficiency
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: mNAPSI scores improvement
Endpoint domain: Physiological/clinical
Endpoint subdomain: General outcomes
Primary endpoint: Patient's global assessment scores
Endpoint domain: Life impact
Endpoint subdomain: Perceived health status
Primary endpoint: VMO: VL activity ratio
Endpoint domain: Physiological/clinical
Endpoint subdomain: Musculoskeletal and connective tissue outcomes
Primary endpoint: Cumulative number of patients
Endpoint domain: Mortality/survival