Cut and Paste: Treating Spinal Muscular Atrophy with Nusinersen
Channel: YourekaScience
Date: 2016-12-26

http://yourekascience.org/portfolio/cut-and-paste-treating-spinal-muscular-atrophy/

In order to make protein, the gibberish portions of RNA are removed to create a coherent message. This is called RNA splicing. RNA splicing of a specific gene is defective in Spinal Muscular Atrophy. Find out how a new drug called "nusinersen" is attempting to repair this splicing defect.

This video was produced in collaboration with Cold Spring Harbor Laboratory.