Haemophilia gene therapy breakthrough (UCL)
Channel: UCL
Date: 2011-12-09

A gene therapy study developed by Dr Amit Nathwani (UCL Cancer Institute) and colleagues in collaboration with St. Jude Children's Research Hospital, Memphis, Tennessee, has shown that adults with haemophilia B benefit from the treatment, reducing need for injections with clotting factor to prevent bleeds. The findings of the six-person study mark the first evidence that gene therapy can reduce disabling, painful bleeding episodes in patients with the inherited blood disorder.

Further information:
Downloadable audio podcast: http://bit.ly/tpgZ4e
BBC News: http://bit.ly/sMPUHn
New York Times: http://bit.ly/twldkJ  
UCL press release: http://bit.ly/v5xtmE

UCL is consistently ranked as one of the world's very best universities. As a multi-faculty, research-intensive university in central London, our research helps tackle global challenges and feeds directly into outstanding degree programmes. Visit us at www.ucl.ac.uk