Treatment evolution in spinal muscular atrophy: insights from the SMArtCARE registry
Year: 2025
Type: article
Language: en
Topic: Neurogenetic and Muscular Disorders Research
Authors and affiliations:
raw_author_name: Cornelia Voigt-Müller
raw_affiliation_strings: Department of Neuropediatrics and Muscle Disorders, Medical Center—University of Freiburg, Faculty of Medicine, University of Freiburg , Freiburg D-79106 ,
raw_author_name: Michelle Pfaffenlehner
raw_affiliation_strings: Faculty of Medicine and Medical Center—University of Freiburg, Institute of Medical Biometry and Statistics , Freiburg D-79104 ,
Freiburg Center for Data Analysis and Modeling and AI, University of Freiburg , Freiburg D-70104 ,
raw_author_name: Günther Bernert
raw_affiliation_strings: Neuromuscular Research Division, Department of Paediatrics and Adolescent Medicine, University Hospital Vienna , Vienna A-1090, Austria
raw_author_name: Hakan Cetin
raw_affiliation_strings: Comprehensive Center for Clinical Neurosciences and Mental Health, Medical University of Vienna , Vienna A-1090 ,
Department of Neurology, Medical University of Vienna , Vienna A-1090 ,
raw_author_name: Tim Hagenacker
raw_affiliation_strings: Department of Neurology, and Center for Translational Neuro- and Behavioral Sciences (C-TNBS), University Medicine Essen , Essen D-45147 ,
raw_author_name: Heike Kölbel
raw_affiliation_strings: Department of Neuropediatrics and Neuromuscular Centre for Children and Adolescents, University of Duisburg-Essen , Essen D-45147 ,
raw_author_name: Hanns Lochmüller
raw_affiliation_strings: Children’s Hospital of Eastern Ontario Research Institute; Division of Neurology, Department of Medicine, The Ottawa Hospital; and Brain and Mind Research Institute, University of Ottawa , Ottawa, ON K1N 6N5 ,
raw_author_name: Christian Pfeuffer
raw_affiliation_strings: Deutsche Gesellschaft für Muskelkranke , Freiburg D-79112 ,
raw_author_name: Katharina Vill
raw_affiliation_strings: Department of Pediatric Neurology and Developmental Medicine and LMU Center for Children with Medical Complexity, Dr. von Hauner Children’s Hospital, LMU Hospital, Ludwig-Maximilians-University , Munich D-80337 ,
raw_author_name: Maggie C Walter
raw_affiliation_strings: Friedrich-Baur-Institute, Department of Neurology, Ludwig-Maximilians-University of Munich , Munich D-80336 ,
raw_author_name: Janbernd Kirschner
raw_affiliation_strings: Department of Neuropediatrics and Muscle Disorders, Medical Center—University of Freiburg, Faculty of Medicine, University of Freiburg , Freiburg D-79106 ,
raw_author_name: Astrid Pechmann
raw_affiliation_strings: Department of Neuropediatrics and Muscle Disorders, Medical Center—University of Freiburg, Faculty of Medicine, University of Freiburg , Freiburg D-79106 ,
raw_author_name: SMArtCARE study group
raw_author_name: Pascal Martin
raw_author_name: Christoph Neuwirth
raw_author_name: Andreas Merkenschlager
raw_author_name: René Günther
raw_author_name: Mathias Müller
raw_author_name: Regina Trollmann
raw_author_name: Gert Wiegand
raw_author_name: Sabine Illsinger
raw_author_name: Omar Keritam
raw_author_name: Matthias Baumann
raw_author_name: Sarah Bernsen
raw_author_name: Claudia Weiß
raw_author_name: Gerd Meyer zu Hörste
raw_author_name: Matthias Türk
raw_author_name: Daniel Zeller
raw_author_name: Thomas M K Völkl
raw_author_name: Uta Diebold
raw_author_name: Verena Haug
raw_author_name: Wolfgang Löscher
raw_author_name: Dorothea Holzwarth
raw_author_name: Mareike Schimmel
raw_author_name: Burkhard Stüve
raw_author_name: Karin Wabnegger
raw_author_name: Ralf A Husain
raw_author_name: Oliver Schwartz
raw_author_name: Matthias Vorgerd
raw_author_name: Eva Matzker
raw_author_name: Gilbert Wunderlich
raw_author_name: Raffi Topakian
raw_author_name: Eckard Hamelmann
raw_author_name: Anette Schwerin-Nagel
raw_author_name: Marina Flotats-Bastardas
raw_author_name: Astrid Blaschek
raw_author_name: Christof Reihle
raw_author_name: Astrid Bertsche
raw_author_name: Ruth Janßen
raw_author_name: Andreas Merkenschlager
raw_author_name: Sandra Nebgen
raw_author_name: Martin Smitka
raw_author_name: Andreas Ziegler
raw_author_name: Manuela Theophil
raw_author_name: Ruth Janßen
raw_author_name: Moritz Metelmann
raw_author_name: Birgit Kauffmann
raw_author_name: Andreas Hahn
raw_author_name: Gudrun Schreiber
raw_author_name: Anette Schwerin-Nagel
raw_author_name: Astrid Eisenkölbl
raw_author_name: Martin Winterholler
raw_author_name: Eva Stögmann
raw_author_name: Veronka Horber
raw_author_name: Friedrich Ebinger
raw_author_name: Tobias Geis
raw_author_name: Martin Fleger
raw_author_name: Jessika Johannsen
raw_author_name: Meike Bettina Göricke
raw_author_name: Veronika Pilshofer
raw_author_name: Maren Fuchs
raw_author_name: Paul Lingor
raw_author_name: Alexander Mensch
raw_author_name: Robert Steinbach
raw_author_name: Sebastian Friedrich
raw_author_name: Julian Großkreutz
raw_author_name: Zeljko Uzelac
raw_author_name: Friederike Sophie Kohlmann
raw_author_name: Harald Faninger
raw_author_name: Simone Mahal
raw_author_name: Christoph Korenke
raw_author_name: Harald Binder
raw_author_name: Katharina Dörnbrack
raw_author_name: Jasmin Bischofberger
raw_author_name: Janina Gburek-Augustat
raw_author_name: Hanna Sophie Lapp
raw_author_name: Tanja Zindler
raw_author_name: Bettina Behring
raw_author_name: Miriam Hiebeler
raw_author_name: Hans Hartmann
raw_author_name: Benjamin Stolte
raw_author_name: Bernhard Fasching
raw_author_name: Christian Lechner
raw_author_name: Patrick Weydt
raw_author_name: Joanna Schneider
raw_author_name: Sarah Wiethoff
raw_author_name: Julia Bellut
raw_author_name: Johannes C Stoffels
raw_author_name: Antje Schmidt
raw_author_name: Corrine G C Horlings