Gene-corrected regulatory T cell therapy for IL2RA deficiency
Year: 2025
Type: article
Language: en
Topic: Immunodeficiency and Autoimmune Disorders
Authors and affiliations:
raw_author_name: Alvin S. Ha
raw_affiliation_strings: Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA 94158, USA
Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA, USA 94143; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA USA 94158
raw_author_name: Nechama Kalter
raw_affiliation_strings: The Institute for Advanced Materials and Nanotechnology, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat Gan 5290002, Israel
The Institute for Advanced Materials and Nanotechnology, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat Gan, Israel 5290002
raw_author_name: Michael Rosenberg
raw_affiliation_strings: The Institute for Advanced Materials and Nanotechnology, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat Gan 5290002, Israel
The Institute for Advanced Materials and Nanotechnology, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat Gan, Israel 5290002
raw_author_name: Luis A. Acevedo
raw_affiliation_strings: Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA
Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA, USA 94143
raw_author_name: Brianna Liang
raw_affiliation_strings: Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA
Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA, USA 94143
raw_author_name: Weihong Liu
raw_affiliation_strings: Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA
Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA, USA 94143
raw_author_name: Sreenivasan Paruthiyil
raw_affiliation_strings: Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA
Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA, USA 94143
raw_author_name: Meenal Sinha
raw_affiliation_strings: Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA
Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA, USA 94143
raw_author_name: Alexander Vu
raw_affiliation_strings: Diabetes Center, University of California, San Francisco, San Francisco, CA 94143, USA; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA 94158, USA
Diabetes Center, University of California San Francisco, San Francisco, CA, USA 94143; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA USA 94158
raw_author_name: Vinh Nguyen
raw_affiliation_strings: Diabetes Center, University of California, San Francisco, San Francisco, CA 94143, USA
Diabetes Center, University of California San Francisco, San Francisco, CA, USA 94143
raw_author_name: Zhongxia Qi
raw_affiliation_strings: Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA
Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA, USA 94143
raw_author_name: Netravathi Krishnappa
raw_affiliation_strings: The Innovative Genomics Institute, University of California, Berkeley, Berkeley, CA 94720, USA
The Innovative Genomics Institute, University of California, Berkeley, Berkeley, CA, USA 94720
raw_author_name: Jinna Shu
raw_affiliation_strings: Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA
Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA, USA 94143
raw_author_name: Jingwei Yu
raw_affiliation_strings: Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA
Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA, USA 94143
raw_author_name: Jason Catanzaro
raw_affiliation_strings: Department of Immunobiology and Internal Medicine, Yale University, New Haven, CT 06520, USA
Department of Immunobiology and Internal Medicine, Yale University, New Haven, CT, USA 06520
raw_author_name: Jeffrey A. Bluestone
raw_affiliation_strings: Sonoma Biotherapeutics, South San Francisco, CA 94080, USA
Sonoma Biotherapeutics, South San Francisco, CA, USA 94080
raw_author_name: Qizhi Tang
raw_affiliation_strings: Diabetes Center, University of California, San Francisco, San Francisco, CA 94143, USA; Department of Surgery, University of California, San Francisco, San Francisco, CA 94143, USA; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA 94158, USA
Diabetes Center, University of California San Francisco, San Francisco, CA, USA 94143; Department of Surgery, University of California, San Francisco, San Francisco, CA, USA 94143; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA USA 94158
raw_author_name: Fyodor D. Urnov
raw_affiliation_strings: Department of Molecular and Cell Biology, University of California, Berkeley, Berkeley, CA 94720, USA; The Innovative Genomics Institute, University of California, Berkeley, Berkeley, CA 94720, USA
Department of Molecular and Cell Biology, University of California, Berkeley, Berkeley, CA, USA 94720; The Innovative Genomics Institute, University of California, Berkeley, Berkeley, CA, USA 94720
raw_author_name: Alexander Marson
raw_affiliation_strings: Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA 94158, USA
Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA USA 94158
raw_author_name: Ayal Hendel
raw_affiliation_strings: The Institute for Advanced Materials and Nanotechnology, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat Gan 5290002, Israel
The Institute for Advanced Materials and Nanotechnology, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat Gan, Israel 5290002
raw_author_name: Kevan C. Herold
raw_affiliation_strings: Department of Immunobiology and Internal Medicine, Yale University, New Haven, CT 06520, USA
Department of Immunobiology and Internal Medicine, Yale University, New Haven, CT, USA 06520
raw_author_name: Brian R. Shy
raw_affiliation_strings: Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA 94158, USA. Electronic address: brian.shy@ucsf.edu
Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA, USA 94143; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA USA 94158. Electronic address: Brian.Shy@ucsf.edu
raw_author_name: Jonathan H. Esensten
raw_affiliation_strings: Advanced Biotherapy Center, Sheba Medical Center, Ramat Gan 5266202, Israel. Electronic address: jonathan.esensten@sheba.health.gov.il
Advanced Biotherapy Center, Sheba Medical Center, Ramat Gan, Israel 5266202. Electronic address: Brian.Shy@ucsf.edu