Patent ID: 11951121
Assignee: VOYAGER THERAPEUTICS, INC.
Field: Pharmaceuticals (Chemistry)
Classification: CPC A  C | IPC A  C

Claim 20:
21. The method of claim 17, wherein the expression of an HTT gene, mRNA, and/or protein is inhibited in a CNS cell or a CNS region, wherein:
(i) the CNS cell comprises a neuron, a medium spiny neuron, an astrocyte, or a combination thereof;
(ii) the CNS region is a forebrain region, a midbrain region, a putamen region, a striatum region, a cortex region, a motor cortex region, a somatosensory cortex region, a temporal cortex region, or a combination thereof; or
(iii) the CNS region is a putamen region.